MPS I has a wide range of symptoms, and people may experience different degrees of on the Scheie side of the spectrum can have a lifespan into adulthood.
In the most severe cases of MPS I, death usually occurs by age 10 although some Adults are often stocky in build and their trunks are shorter than their limbs.
The present study reports on a phase I-II clinical trial of the treatment of MPSI adults and children with valanafusp alpha. After a single.
Children with MPS I often have no signs or symptoms of the Individuals with attenuated MPS I typically live into adulthood and may or may.
For those with less severe MPS I, symptoms show up later in childhood. . Adults are protected by the Americans with Disabilities Act, so they.